PTC Therapeutics - PharmaKB

Company Reports

Company Reports

Disease Reports

Disease Reports

Company ReportsPTC Therapeutics

PTC Therapeutics(PTCT)

PTC Therapeutics is a US pharmaceutical company focused on the development of orally administered small molecule drugs and gene therapy which regulate gene expression by targeting post-transcriptional control (PTC) mechanisms in orphan diseases.

Download report

Favorite

Financial

Marketed Drugs

Clinical Trials

Financial

Stock price

*Currency in USD

Company Revenue

Quarterly

Quarterly

Annual

Annual

Projections

*Quarterly sales USD (in millions)

Plot placeholder

Mock data
Subscribe for the real data

Revenue by Drug

Marketed Drugs

Therapeutic Areas:

All

Classification:

All

Include Generics:

Trade Name	Drug Name	Approved	Patent Expires	Indication
Emflaza	Deflazacort	2017-02-09		Inflammation , Duchenne muscular dystrophy
Translarna	Ataluren	2014-07-31		Duchenne muscular dystrophy
Upstaza	Eladocagene exuparvovec	2022-07-18		Inborn errors amino acid metabolism

Clinical Trials

Therapeutic Areas:

All

Classification:

All

Approval:

All

Status:

All

Phases:

All

Drug Name

Phase 1

Phase 2

Phase 3

Phase 4

Indication

ELADOCAGENE EXUPARVOVEC

argininosuccinic aciduria

,

breast neoplasms

,

central nervous system neoplasms

,

nervous system neoplasms

,

,

myeloid leukemia acute

,

myeloid leukemia

,

,

,

neurofibromatosis 2

,

neurofibromatosis 1

,

neurofibromatoses

,

,

,

coronavirus infections

,

,

,

,

allergic rhinitis

,

,

allergic conjunctivitis

,

liver neoplasms

,

atopic dermatitis

,

,

healthy volunteers/patients

,

,

,

,

,

prostatic neoplasms

,

postoperative nausea and vomiting

,

,

brain neoplasms

,

second primary neoplasms

,

,

treatment-resistant depressive disorder

,

depressive disorder

,

esophageal neoplasms

,

esophageal squamous cell carcinoma

,

hematologic neoplasms

,

,

pseudomonas infections

,

pseudomonas aeruginosa

,

,

renal cell carcinoma

,

liver cirrhosis

,

experimental liver cirrhosis

,

chronic obstructive pulmonary disease

,

nasopharyngeal carcinoma

,

nasopharyngeal neoplasms

,

ovarian epithelial carcinoma

,

,

colorectal neoplasms

,

pancreatic ductal carcinoma

,

gastrointestinal neoplasms

,

biliary tract neoplasms

,

non-small-cell lung carcinoma

,

,

,

,

acquired immunodeficiency syndrome

,

ovarian neoplasms

,

breast neoplasms

,

,

hepatocellular carcinoma

,

,

immunologic deficiency syndromes

,

,

antibiotic prophylaxis

,

,

chronic hepatitis b

,

uterine cervical neoplasms

,

condylomata acuminata

,

coronary disease

,

coronary artery disease

,

myocardial ischemia

,

,

,

cystic fibrosis

,

pulmonary hypertension

,

pulmonary arterial hypertension

,

endometrial neoplasms

,

,

triple negative breast neoplasms

,

,

chronic hepatitis c

,

,

,

,

,

neuromuscular blockade

,

chronic kidney failure

,

kidney diseases

,

chronic hepatitis

,

,

intestinal diseases

,

non-hodgkin lymphoma

,

,

,

traumatic brain injuries

,

brain concussion

,

,

post-concussion syndrome

renal cell carcinoma

,

human influenza

,

nutritional status

,

pneumococcal infections

,

pneumococcal pneumonia

,

,

,

systemic lupus erythematosus

,

cutaneous lupus erythematosus

,

inflammatory bowel diseases

,

,

,

tendon injuries

,

,

haemophilus influenzae

,

streptococcus pneumoniae

,

,

,

,

energy metabolism

,

endometrial neoplasms

,

,

mullerian mixed tumor

,

,

idiopathic pulmonary fibrosis

,

pulmonary fibrosis

,

,

non-small-cell lung carcinoma

,

,

neoplasm metastasis

,

,

falciparum malaria

,

ovarian neoplasms

,

brain neoplasms

,

healthy volunteers/patients

,

prostatic neoplasms

,

,

,

colorectal neoplasms

,

squamous cell carcinoma

,

multiple myeloma

,

plasma cell neoplasms

,

ovarian epithelial carcinoma

,

cutaneous malignant melanoma

,

,

type 1 diabetes mellitus

,

triple negative breast neoplasms

,

squamous cell carcinoma of head and neck

,

sickle cell anemia

,

myeloid leukemia acute

,

myeloid leukemia

,

,

,

chronic hepatitis b

,

,

primary myelofibrosis

,

hepatocellular carcinoma

,

liver neoplasms

,

fallopian tube neoplasms

,

pancreatic neoplasms

,

,

hematologic neoplasms

,

ductal carcinoma

,

circulating neoplastic cells

,

uterine neoplasms

,

uterine cervical neoplasms

,

,

streptococcus agalactiae

,

,

follicular lymphoma

,

neisseria meningitidis

,

haemophilus influenzae type b

,

invasive hydatidiform mole

,

biliary tract neoplasms

,

uveal neoplasms

,

respiratory tract diseases

,

respiration disorders

,

,

focal segmental glomerulosclerosis

,

cytomegalovirus infections

,

chronic hepatitis

,

kidney diseases

,

membranous glomerulonephritis

,

nephrotic syndrome

,

,

,

endometrioid carcinoma

,

breast diseases

,

squamous cell neoplasms

,

neurofibromatosis 2

,

acoustic neuroma

,

neurofibromatosis 1

,

neurofibromatoses

,

,

,

,

,

pulmonary tuberculosis

,

adenocarcinoma of lung

,

disease progression

,

peritoneal neoplasms

,

,

beta-thalassemia

,

,

sickle cell trait

,

essential thrombocythemia

,

polycythemia vera

,

,

,

,

,

breast neoplasms

,

,

rheumatoid arthritis

,

,

head and neck neoplasms

,

inflammatory breast neoplasms

,

,

respiratory syncytial virus infections

,

,

bacterial infections

,

,

streptococcal infections

,

,

stomach neoplasms

,

gastrointestinal neoplasms

,

digestive system neoplasms

,

infectious skin diseases

,

bacterial skin diseases

,

ductal carcinoma breast

,

renal insufficiency

,

,

,

,

urinary bladder neoplasms

,

acute coronary syndrome

,

,

rotavirus infections

,

,

mucinous adenocarcinoma

,

,

meningococcal meningitis

,

,

respiratory syncytial viruses

,

,

,

type 2 diabetes mellitus

,

diabetes mellitus

,

,

,

acquired immunodeficiency syndrome

,

,

chronic obstructive pulmonary disease

,

communicable diseases

,

,

obstructive lung diseases

,

,

dental focal infection

,

focal infection

,

,

,

immunologic deficiency syndromes

,

ventilator-associated pneumonia

,

growth and development

,

immunologic tests

,

,

alzheimer disease

,

wasting syndrome

,

,

,

insulin resistance

,

abdominal obesity

,

lipid metabolism

,

latent autoimmune diabetes in adults

,

community-acquired infections

,

,

,

staphylococcal infections

,

resistance training

,

,

,

major depressive disorder

,

depressive disorder

,

thyroid neoplasms

,

papillary thyroid cancer

,

thyroid diseases

,

clostridioides difficile

,

open-angle glaucoma

,

alzheimer disease

,

,

myocardial infarction

,

,

,

renal cell carcinoma

,

ovarian neoplasms

,

urinary bladder neoplasms

,

fallopian tube neoplasms

,

,

ovarian epithelial carcinoma

,

,

,

barrett esophagus

,

chronic progressive multiple sclerosis

,

vitamin d deficiency

,

hypersensitivity

,

oral lichen planus

,

,

epidermolysis bullosa

,

,

,

,

,

sleep apnea syndromes

,

vestibular diseases

,

,

,

keratoconjunctivitis sicca

,

dry eye syndromes

,

,

retinal diseases

,

diabetic retinopathy

,

,

stomach neoplasms

,

pancreatic neoplasms

,

,

,

multiple sclerosis

,

,

amyotrophic lateral sclerosis

,

motor neuron disease

,

,

bipolar disorder

,

,

,

non-small-cell lung carcinoma

,

precursor cell lymphoblastic leukemia-lymphoma

,

second primary neoplasms

,

type 2 diabetes mellitus

,

chromosome deletion

,

type 1 diabetes mellitus

,

diastolic heart failure

,

,

cystic fibrosis

,

,

renal insufficiency

,

squamous cell carcinoma

,

squamous cell neoplasms

,

,

post-acute covid-19 syndrome

,

,

,

burkitt lymphoma

,

,

thrombocytopenia

,

,

lactic acidosis

,

,

mantle-cell lymphoma

,

lymphoid leukemia

,

aids-related lymphoma

,

spinal cord injuries

,

prader-willi syndrome

,

post-cardiac arrest syndrome

,

,

pulmonary tuberculosis

,

rectal neoplasms

,

cri-du-chat syndrome

,

macrocytic anemia

,

,

chronic hepatitis b

,

,

chronic hepatitis

,

,

atopic dermatitis

,

,

,

,

noise-induced hearing loss

,

,

,

sudden death cardiac

,

,

basal cell carcinoma

,

nerve compression syndromes

,

,

charcot-marie-tooth disease

,

hereditary sensory and motor neuropathy

,

,

bipolar and related disorders

,

,

,

metabolic diseases

,

,

glycogen storage disease type ii

,

lysosomal storage diseases

,

glycogen storage disease

,

,

,

,

mitochondrial diseases

,

healthy volunteers/patients

,

parkinson disease

,

colorectal neoplasms

,

chronic fatigue syndrome

,

,

,

breast neoplasms

,

coronary artery disease

,

,

polycystic ovary syndrome

,

prostatic neoplasms

,

cerebellar ataxia

,

huntington disease

,

myocardial ischemia

,

,

,

,

friedreich ataxia

,

,

,

progressive supranuclear palsy

,

duchenne muscular dystrophy

,

muscular dystrophies

,

myelodysplastic syndromes

,

coronary disease

,

drug-related side effects and adverse reactions

,

non-alcoholic fatty liver disease

,

,

cognitive dysfunction

,

cholangiocarcinoma

,

liver neoplasms

,

neoplasm metastasis

,

,

biliary tract neoplasms

,

t-cell lymphoma

,

t-cell lymphoma peripheral

,

,

,

persian gulf syndrome

,

,

hyperlipidemias

,

hyperlipoproteinemias

,

,

,

gastrointestinal neoplasms

,

neuroendocrine tumors

,

carcinoid tumor

,

paraneoplastic syndromes

,

islet cell adenoma

,

malignant carcinoid syndrome

,

rem sleep behavior disorder

,

mental disorders

,

headache disorders

,

nervous system diseases

,

hepatocellular carcinoma

,

gallbladder neoplasms

,

ampulla of vater cancer

,

pathologic dilatation

,

,

corneal diseases

,

,

multiple organ failure

,

,

,

limb-girdle muscular dystrophies

,

,

coronary artery bypass

,

cardiac valve annuloplasty

,

,

coronary stenosis

,

,

juvenile arthritis

,

,

,

,

myotonic dystrophy

,

,

,

cardiovascular diseases

,

male infertility

,

hypercholesterolemia

,

,

migraine disorders

,

diabetes mellitus

,

metabolic syndrome

,

oxidative stress

,

kidney diseases

,

,

atherosclerosis

,

,

,

,

chronic kidney failure

,

insulin resistance

,

,

,

,

hypertriglyceridemia

,

,

chronic renal insufficiency

,

critical illness

,

,

opioid-related disorders

,

morphine dependence

,

,

,

,

,

muscle weakness

,

cardiomyopathies

,

dilated cardiomyopathy

,

,

severe acute respiratory syndrome-related coronavirus

,

severe acute respiratory syndrome

,

,

,

,

temporomandibular joint disorders

,

,

temporomandibular joint dysfunction syndrome

,

acute coronary syndrome

,

attitudes health knowledge practice

,

postoperative pain

,

periodontal diseases

,

,

,

,

,

muscular diseases

,

depressive disorder

,

,

myofascial pain syndromes

,

,

,

medication adherence

,

chromosome disorders

,

autistic disorder

,

autism spectrum disorder

,

,

fetal growth retardation

,

premature birth

,

iron deficiencies

,

vitamin b 12 deficiency

,

,

dermatomyositis

,

,

female infertility

,

,

cardiovascular abnormalities

,

ascorbic acid deficiency

,

ovarian reserve

,

vascular remodeling

,

macular degeneration

,

wet macular degeneration

,

,

post-concussion syndrome

,

gestational diabetes

,

pregnancy outcome

,

gingival recession

,

acute kidney injury

,

intellectual disability

,

hepatic encephalopathy

,

psychotic disorders

,

health status indicators

,

aphthous stomatitis

,

,

,

,

attention deficit disorder with hyperactivity

,

,

mitochondrial genome

,

reproductive physiological phenomena

,

inborn genetic diseases

,

pulmonary arterial hypertension

,

familial primary pulmonary hypertension

,

spontaneous abortion

,

,

kidney transplantation

,

ischemic preconditioning

,

,

respiratory tract infections

,

encephalomyelitis

,

dietary supplements

,

,

,

dental implants

,

,

,

chronic periodontitis

,

,

,

,

physical fitness

,

liver cirrhosis

,

,

st elevation myocardial infarction

,

,

ovarian neoplasms

,

ovarian epithelial carcinoma

,

,

diffuse intrinsic pontine glioma

,

,

,

b-cell chronic lymphocytic leukemia

,

lymphoid leukemia

,

,

,

,

,

,

atopic dermatitis

,

,

,

ischemic optic neuropathy

,

follicular lymphoma

,

large b-cell lymphoma diffuse

,

b-cell lymphoma

,

non-small-cell lung carcinoma

,

,

non-hodgkin lymphoma

,

bullous pemphigoid

,

kidney diseases

,

,

lupus nephritis

,

,

,

giant cell arteritis

,

polymyalgia rheumatica

,

systemic lupus erythematosus

,

neuromyelitis optica

,

,

,

,

breast neoplasms

,

hand-foot syndrome

,

myasthenia gravis

,

muscle weakness

,

,

,

multiple sclerosis

,

relapsing-remitting multiple sclerosis

,

chronic progressive multiple sclerosis

,

,

,

kidney transplantation

,

,

rheumatoid arthritis

,

liver transplantation

,

juvenile arthritis

,

heart transplantation

,

hypersensitivity

huntington disease

non-hodgkin lymphoma

,

kidney transplantation

,

graft rejection

,

,

,

precursor cell lymphoblastic leukemia-lymphoma

,

lymphoid leukemia

,

multiple myeloma

,

plasma cell neoplasms

,

,

juvenile arthritis

,

colonic neoplasms

,

non-hodgkin lymphoma

,

pharmacokinetics

,

hematologic neoplasms

,

b-cell chronic lymphocytic leukemia

,

neoplasm micrometastasis

,

neuroendocrine tumors

,

medical sociology

,

thrombocytopenia

,

connective and soft tissue neoplasms

,

paraneoplastic syndromes

,

,

renal insufficiency

,

vaginal neoplasms

,

vulvar neoplasms

,

rectal neoplasms

,

,

,

,

colorectal neoplasms

,

,

kidney neoplasms

,

liver neoplasms

,

,

biliary tract neoplasms

,

,

,

hepatocellular carcinoma

,

thyroid neoplasms

,

,

,

gallbladder neoplasms

,

cholangiocarcinoma

,

pleural effusion

,

malignant pleural effusion

,

,

,

adenosquamous carcinoma

,

gastrointestinal stromal tumors

,

,

hemangiosarcoma

,

hyperthermic intraperitoneal chemotherapy

,

synovial sarcoma

,

urogenital neoplasms

,

thymus neoplasms

,

small cell carcinoma

,

dna repair-deficiency disorders

,

thyroid diseases

,

uterine neoplasms

,

myeloid leukemia acute

,

,

,

carcinoma in situ

,

,

germ cell and embryonal neoplasms

,

,

large cell carcinoma

,

,

papillomaviridae

,

neuroendocrine carcinoma

,

residual neoplasm

,

,

,

cognitive dysfunction

,

myeloproliferative disorders

,

multiple myeloma

,

alopecia areata

,

,

lacrimal apparatus diseases

,

adrenocortical carcinoma

,

,

heavy ion radiotherapy

,

merkel cell carcinoma

,

microsatellite instability

,

breast carcinoma in situ

,

lobular carcinoma

,

testicular neoplasms

,

branchio-oto-renal syndrome

,

,

,

,

left ventricular dysfunction

,

ventricular dysfunction

,

,

,

somatoform disorders

,

disseminated intravascular coagulation

,

tonsillar neoplasms

,

glandular and epithelial neoplasms

,

,

cardiovascular diseases

,

,

intraductal carcinoma noninfiltrating

,

anaplastic thyroid carcinoma

,

antineoplastic combined chemotherapy protocols

,

,

urologic diseases

,

urinary bladder diseases

,

,

papillomavirus infections

,

neurofibrosarcoma

,

nerve sheath neoplasms

,

lymphatic metastasis

,

,

bone marrow diseases

,

epstein-barr virus infections

,

,

hormone-dependent neoplasms

,

ampulla of vater cancer

,

gastrointestinal diseases

,

digestive system diseases

,

mycobacterium infections

,

mediastinal neoplasms

,

palliative care

,

mullerian mixed tumor

,

pancoast syndrome

,

penile neoplasms

,

thromboembolism

,

intestinal neoplasms

,

myelodysplastic syndromes

,

precancerous conditions

,

plasma cell neoplasms

,

,

,

,

central nervous system neoplasms

,

nervous system neoplasms

,

adenoid cystic carcinoma

,

intestinal obstruction

,

alphapapillomavirus

,

carcinoid tumor

,

,

pancreatic ductal carcinoma

,

hodgkin disease

,

maxillary sinus neoplasms

,

adolescent development

,

,

cancer vaccines

,

radiation effects

,

perioperative period

,

,

ovarian neoplasms

,

nasopharyngeal carcinoma

,

,

nasopharyngeal neoplasms

,

,

ovarian epithelial carcinoma

,

pancreatic neoplasms

,

urinary bladder neoplasms

,

esophageal squamous cell carcinoma

,

urologic neoplasms

,

transitional cell carcinoma

,

fallopian tube neoplasms

,

hypersensitivity

,

uterine cervical neoplasms

,

peritoneal neoplasms

,

small cell lung carcinoma

,

laryngeal neoplasms

,

endometrial neoplasms

,

oropharyngeal neoplasms

,

,

renal cell carcinoma

,

hypopharyngeal neoplasms

,

inflammatory breast neoplasms

,

salivary gland neoplasms

,

mouth neoplasms

,

,

,

chemotherapy-induced febrile neutropenia

,

disease progression

,

neoadjuvant therapy

,

non-muscle invasive bladder neoplasms

,

invasive hydatidiform mole

,

laryngeal diseases

,

drug-related side effects and adverse reactions

,

gastrointestinal neoplasms

,

,

,

unknown primary neoplasms

,

ureteral neoplasms

,

malignant fibrous histiocytoma

,

,

tongue neoplasms

,

digestive system neoplasms

,

urethral neoplasms

,

brain stem neoplasms

,

paranasal sinus neoplasms

,

circulating neoplastic cells

,

endometrioid carcinoma

,

breast diseases

,

bronchiolo-alveolar adenocarcinoma

,

hereditary breast and ovarian cancer syndrome

,

disease-free survival

,

verrucous carcinoma

,

brain neoplasms

,

cystadenocarcinoma

,

chemoradiotherapy

,

rhabdomyosarcoma

,

,

mucinous cystadenocarcinoma

,

mucinous adenocarcinoma

,

serous cystadenocarcinoma

,

clear cell adenocarcinoma

,

neoplasms by site

,

local neoplasm recurrence

,

ductal carcinoma breast

,

bronchogenic carcinoma

,

ductal carcinoma

,

neurotoxicity syndromes

,

healthy volunteers/patients

,

,

progression-free survival

,

postoperative complications

,

,

acinar cell carcinoma

,

,

pelvic neoplasms

,

induction chemotherapy

,

respiratory tract diseases

,

,

respiratory tract neoplasms

,

thoracic neoplasms

,

bronchial neoplasms

,

genetic predisposition to disease

,

disease susceptibility

,

,

pharyngeal neoplasms

,

wasting syndrome

,

,

,

therapeutic equivalency

,

adenomyoepithelioma

,

,

directly observed therapy

,

alveolar rhabdomyosarcoma

,

embryonal rhabdomyosarcoma

,

breast neoplasms

,

non-small-cell lung carcinoma

,

,

prostatic neoplasms

,

,

,

stomach neoplasms

,

,

squamous cell carcinoma

,

esophageal neoplasms

,

squamous cell carcinoma of head and neck

,

head and neck neoplasms

,

castration-resistant prostatic neoplasms

,

triple negative breast neoplasms

,

neoplasm metastasis

,

squamous cell neoplasms

,

,

adenocarcinoma of lung

,

male breast neoplasms

,

peripheral nervous system diseases

,

febrile neutropenia

,

,

second primary neoplasms

,

wounds and injuries

,

chemical and drug induced liver injury

,

meningeal carcinomatosis

,

,

,

,

,

,

breast cancer lymphedema

,

taste disorders

,

,

,

,

,

prospective studies

,

pharmacogenomic testing

,

,

chemotherapy-related cognitive impairment

,

,

,

,

postoperative pain

,

,

,

,

pathologic complete response

,

hand-foot syndrome

,

intravesical administration

,

mycobacterium bovis

1

2

>

© 2020-2024 Collaborative Drug Discovery Inc. (CDD) | Terms of Use