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PTC Therapeutics
PTC Therapeutics
(PTCT)
PTC Therapeutics is a US pharmaceutical company focused on the development of orally administered small molecule drugs and gene therapy which regulate gene expression by targeting post-transcriptional control (PTC) mechanisms in orphan diseases.
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Therapeutic Areas:
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Include Generics:
Trade Name
Drug Name
Approved
Patent Expires
Indication
Emflaza
Deflazacort
2017-02-09
Inflammation
,
Duchenne muscular dystrophy
Translarna
Ataluren
2014-07-31
Duchenne muscular dystrophy
Upstaza
Eladocagene exuparvovec
2022-07-18
Inborn errors amino acid metabolism
Clinical Trials
Therapeutic Areas:
All
Classification:
All
Approval:
All
Status:
All
Phases:
All
Drug Name
Phase 1
Phase 2
Phase 3
Phase 4
Indication
Ataluren
healthy volunteers/patients
,
aniridia
,
hemophilia a
,
hemophilia b
,
colorectal neoplasms
,
endometrial neoplasms
,
epilepsy
,
myoclonic epilepsies
,
inborn errors metabolism
,
inborn errors amino acid metabolism
,
duchenne muscular dystrophy
,
muscular dystrophies
,
inborn genetic diseases
,
muscular diseases
,
nervous system diseases
,
musculoskeletal diseases
,
x-linked genetic diseases
,
neuromuscular diseases
,
atrophic muscular disorders
,
fibrosis
,
cystic fibrosis
Deflazacort
healthy volunteers/patients
,
renal insufficiency
,
liver diseases
,
hepatic insufficiency
,
muscular dystrophies
,
duchenne muscular dystrophy
,
limb-girdle muscular dystrophies
ELADOCAGENE EXUPARVOVEC
argininosuccinic aciduria
Sepiapterin
gastroparesis
,
phenylketonurias
Vatiquinone
tic disorders
,
tourette syndrome
,
tics
,
alzheimer disease
,
dementia
,
muscular diseases
,
rett syndrome
,
ataxia
,
inborn genetic diseases
,
retinal diseases
,
homocystinuria
,
syndrome
,
inborn errors lipid metabolism
,
noise-induced hearing loss
,
angelman syndrome
,
autistic disorder
,
autism spectrum disorder
,
cerebellar ataxia
,
parkinson disease
,
mitochondrial diseases
,
friedreich ataxia
,
leigh disease
,
melas syndrome
,
diffuse cerebral sclerosis of schilder
,
drug resistant epilepsy
,
merrf syndrome
,
seizures
,
status epilepticus
,
nerve degeneration
,
mitochondrial encephalomyopathies
,
optic nerve diseases
,
emergencies
,
hereditary optic atrophy leber
Emvododstat
neoplasms
,
breast neoplasms
,
central nervous system neoplasms
,
nervous system neoplasms
,
leukemia
,
myeloid leukemia acute
,
myeloid leukemia
,
sarcoma
,
kaposi sarcoma
,
neurofibromatosis 2
,
neurofibromatosis 1
,
neurofibromatoses
,
neurofibroma
,
covid-19
,
coronavirus infections
,
coronavirus
,
pneumonia
Gilvetmab
urinary bladder neoplasms
,
glandular and epithelial neoplasms
,
myoepithelioma
,
hepatitis c
,
hepatitis
,
hepatitis a
,
multiple myeloma
,
neoplasms by histologic type
,
urinary bladder diseases
,
astrocytoma
,
myeloid leukemia acute
,
gata2 deficiency
,
pancreatic neoplasms
,
colorectal neoplasms
,
glioblastoma
,
colonic neoplasms
,
cutaneous malignant melanoma
,
prostatic neoplasms
,
glioma
,
transitional cell carcinoma
,
liver neoplasms
,
small cell lung carcinoma
,
pancreatic ductal carcinoma
,
adenocarcinoma
,
urologic neoplasms
,
stomach neoplasms
,
endometrial neoplasms
,
carcinoma
,
squamous cell carcinoma
,
recurrence
,
neoplasms by site
,
rectal neoplasms
,
ovarian neoplasms
,
chordoma
,
biliary tract neoplasms
,
hepatocellular carcinoma
,
sarcoma
,
microsatellite instability
,
gliosarcoma
,
non-hodgkin lymphoma
,
hodgkin disease
,
uterine cervical neoplasms
,
follicular lymphoma
,
lymphoma
,
squamous cell neoplasms
,
female genital neoplasms
,
endometrioid carcinoma
,
spinocerebellar degenerations
,
neuroendocrine tumors
,
gastrointestinal neoplasms
,
adenocarcinoma of lung
,
basal cell carcinoma
,
basal cell neoplasms
,
nose neoplasms
,
nasopharyngeal carcinoma
,
nasopharyngeal neoplasms
,
t-cell lymphoma peripheral
,
oropharyngeal neoplasms
,
prostatic diseases
,
cholangiocarcinoma
,
diffuse intrinsic pontine glioma
,
hematologic neoplasms
,
b-cell chronic lymphocytic leukemia
,
bile duct neoplasms
,
genetic therapy
,
smoldering multiple myeloma
,
carcinosarcoma
,
urogenital neoplasms
,
small cell carcinoma
,
penile neoplasms
,
adrenocortical carcinoma
,
mesothelioma
,
drug-related side effects and adverse reactions
,
lung diseases
,
precancerous conditions
,
bronchopulmonary dysplasia
,
tobacco smoking
,
b-cell lymphoma marginal zone
,
mantle-cell lymphoma
,
waldenstrom macroglobulinemia
,
large b-cell lymphoma diffuse
,
burkitt lymphoma
,
oligodendroglioma
,
merkel cell carcinoma
,
hereditary nonpolyposis colorectal neoplasms
,
b-cell lymphoma
,
disease
,
melanoma
,
non-small-cell lung carcinoma
,
neoplasms
,
neoplasm metastasis
,
squamous cell carcinoma of head and neck
,
renal cell carcinoma
,
lung neoplasms
,
breast neoplasms
,
head and neck neoplasms
,
brain neoplasms
,
kidney neoplasms
,
triple negative breast neoplasms
,
skin neoplasms
,
fallopian tube neoplasms
,
ovarian epithelial carcinoma
,
pathologic complete response
Alfacalcidol
hepatitis c
,
hepatitis
,
hepatitis a
,
leukemia
,
myeloid leukemia acute
,
recurrence
Aspartame
healthy volunteers/patients
,
alzheimer disease
,
female genital neoplasms
,
melanoma
,
chronic hepatitis b
,
depression
,
major depressive disorder
,
depressive disorder
,
triple negative breast neoplasms
,
pancreatic neoplasms
,
coronary disease
,
coronary artery disease
,
myocardial ischemia
,
heart diseases
,
lung neoplasms
,
sickle cell anemia
,
sarcoma
,
glioma
,
neuroblastoma
,
precursor cell lymphoblastic leukemia-lymphoma
,
parkinson disease
,
autistic disorder
,
autism spectrum disorder
,
pervasive child development disorders
,
chronic hepatitis
,
rectal neoplasms
,
covid-19
,
pneumonia
,
leukemia
,
b-cell chronic lymphocytic leukemia
,
lymphoid leukemia
,
exanthema
,
nasopharyngeal carcinoma
,
nasopharyngeal neoplasms
,
stomach neoplasms
,
esophageal neoplasms
,
adenocarcinoma
,
neoplasm metastasis
,
antiphospholipid syndrome
,
respiratory insufficiency
,
neoplasms
,
colorectal neoplasms
,
non-small-cell lung carcinoma
,
lupus nephritis
,
human influenza
,
breast neoplasms
,
anemia
,
large b-cell lymphoma diffuse
,
b-cell lymphoma
,
non-hodgkin lymphoma
,
myeloid leukemia acute
,
multiple sclerosis
,
nephritis
,
hepatocellular carcinoma
,
colonic neoplasms
,
thrombocytopenic purpura idiopathic
,
liver cirrhosis
,
neuromyelitis optica
,
membranous glomerulonephritis
,
chronic progressive multiple sclerosis
,
relapsing-remitting multiple sclerosis
,
nephrotic syndrome
,
ovarian neoplasms
,
ovarian epithelial carcinoma
,
hemolysis
,
hemolytic anemia autoimmune
,
hepatitis c
,
chronic hepatitis c
,
hepatitis
,
hepatitis a
,
rheumatoid arthritis
,
lymphoma
,
arthritis
,
juvenile arthritis
,
hiv infections
,
follicular lymphoma
,
asthma
,
heart failure
,
myelodysplastic syndromes
,
preleukemia
,
syndrome
,
acquired immunodeficiency syndrome
,
kidney transplantation
,
drug-related side effects and adverse reactions
,
heart disease risk factors
,
cognitive dysfunction
Bevifimod
hematologic neoplasms
,
biphenotypic leukemia acute
,
b-cell leukemia
,
precursor cell lymphoblastic leukemia-lymphoma
,
stomach neoplasms
,
myelodysplastic syndromes
,
stroke
,
muscle spasticity
,
precursor t-cell lymphoblastic leukemia-lymphoma
,
precursor b-cell lymphoblastic leukemia-lymphoma
,
endometriosis
,
infertility
,
b-cell lymphoma
,
ovarian neoplasms
,
recurrence
,
b-cell lymphoma marginal zone
,
fallopian tube neoplasms
,
multiple myeloma
,
prostatic neoplasms
,
pancreatic neoplasms
,
burkitt lymphoma
,
triple negative breast neoplasms
,
esophageal neoplasms
,
squamous cell carcinoma of head and neck
,
reactive arthritis
,
waldenstrom macroglobulinemia
,
lymphoproliferative disorders
,
lymphatic diseases
,
intestinal neoplasms
,
colonic neoplasms
,
rectal neoplasms
,
carcinoma
,
glioblastoma
,
melanoma
,
neuroendocrine carcinoma
,
papillary thyroid cancer
,
adenocarcinoma
,
primary myelofibrosis
,
splenomegaly
,
hairy cell leukemia
,
abdominal hernia
,
ventral hernia
,
breast neoplasms
,
urinary bladder neoplasms
,
uterine neoplasms
,
knee osteoarthritis
,
residual neoplasm
,
neuralgia
,
interstitial cystitis
,
neoadjuvant therapy
,
ovarian epithelial carcinoma
,
mantle-cell lymphoma
,
female genital neoplasms
,
peritoneal neoplasms
,
neoplasms
,
non-hodgkin lymphoma
,
crohn disease
,
non-small-cell lung carcinoma
,
b-cell chronic lymphocytic leukemia
,
lymphoma
,
myeloid leukemia acute
,
colorectal neoplasms
,
large b-cell lymphoma diffuse
,
follicular lymphoma
,
lung neoplasms
,
joint diseases
,
musculoskeletal diseases
,
ankylosing spondylitis
,
small cell lung carcinoma
,
multiple sclerosis
,
relapsing-remitting multiple sclerosis
,
inflammatory bowel diseases
,
macular degeneration
,
lymphoid leukemia
,
spondylitis
,
juvenile arthritis
,
neoplasm metastasis
,
skin diseases
,
papulosquamous skin diseases
,
wet macular degeneration
,
leukemia
,
infections
,
communicable diseases
,
bacterial infections
,
methicillin-resistant staphylococcus aureus
,
staphylococcal skin infections
,
infectious skin diseases
,
bacterial skin diseases
,
cellulitis
,
disease progression
,
covid-19
,
parkinson disease
,
bronchopulmonary dysplasia
,
respiratory syncytial viruses
,
hepatitis b
,
ulcer
,
pyoderma gangrenosum
,
spondylarthropathies
,
spondylarthritis
,
spinal diseases
,
uveitis
,
intermediate uveitis
,
posterior uveitis
,
precocious puberty
,
migraine disorders
,
retinal diseases
,
retinal degeneration
,
eye diseases
,
choroidal neovascularization
,
hepatocellular carcinoma
,
liver neoplasms
,
thyroid diseases
,
hypothyroidism
,
rheumatoid arthritis
,
psoriasis
,
arthritis
,
ulcerative colitis
,
psoriatic arthritis
,
hepatitis c
,
chronic hepatitis c
,
hidradenitis suppurativa
,
axial spondyloarthritis
,
cardiovascular diseases
,
connective tissue diseases
,
seizures
,
panuveitis
,
hiv infections
,
drug monitoring
,
coronary artery disease
,
myocardial ischemia
,
inflammation
,
atherosclerosis
Unesbulin
ovarian neoplasms
,
ovarian epithelial carcinoma
,
glioma
,
diffuse intrinsic pontine glioma
,
neoplasms
,
leiomyosarcoma
Bos taurus adrenal cortex corticosteroids
libido
,
colorectal neoplasms
,
carcinoma
,
hepatocellular carcinoma
,
liver neoplasms
,
chronic renal insufficiency
,
kidney diseases
,
type 2 diabetes mellitus
,
diabetes mellitus
,
atopic dermatitis
,
dermatitis
Lactams
healthy volunteers/patients
,
melanoma
,
urinary tract infections
,
gram-negative bacterial infections
,
neoplasms
,
non-small-cell lung carcinoma
,
triple negative breast neoplasms
,
neoplasm metastasis
,
soft tissue infections
,
genomic instability
,
bacterial pneumonia
,
pancreatic neoplasms
,
urinary bladder neoplasms
,
cholangiocarcinoma
,
ovarian neoplasms
,
brain neoplasms
,
stomach neoplasms
,
inflammatory breast neoplasms
,
patient preference
,
breast neoplasms
,
pneumonia
,
cystic fibrosis
,
pseudomonas infections
,
pseudomonas aeruginosa
,
hiv infections
,
hiv seropositivity
,
neurosyphilis
Mk3475
neoplasms
Solumedrol
pathologic dilatation
,
cardiac arrhythmias
,
intestinal diseases
,
therapeutic equivalency
,
precancerous conditions
,
friedreich ataxia
,
retinal perforations
,
fever
,
tinnitus
,
laser therapy
,
innate immunity
,
immunoglobulin light-chain amyloidosis
,
monoclonal gammopathy of undetermined significance
,
pharmacokinetics
,
pharmacological phenomena
,
aneurysm
,
coronary aneurysm
,
raynaud disease
,
ataxia
,
cerebellar ataxia
,
labor pain
,
allergic contact dermatitis
,
malnutrition
,
biological availability
,
drug hypersensitivity syndrome
,
asymptomatic diseases
,
hyperuricemia
,
retinal telangiectasis
,
closed fractures
,
cohort studies
,
stevens-johnson syndrome
,
facial nerve injuries
,
peripheral nerve injuries
,
gastrointestinal diseases
,
myeloproliferative disorders
,
myelodysplastic-myeloproliferative diseases
,
mantle-cell lymphoma
,
t-cell lymphoma
,
b-cell lymphoma marginal zone
,
myeloid leukemia chronic-phase
,
myelomonocytic leukemia chronic
,
t-cell lymphoma peripheral
,
ovarian neoplasms
,
myeloid leukemia accelerated phase
,
blast crisis
,
fanconi anemia
,
myelomonocytic leukemia juvenile
,
immunoblastic lymphadenopathy
,
congenital abnormalities
,
neuroblastoma
,
t-cell lymphoma cutaneous
,
primary myelofibrosis
,
waldenstrom macroglobulinemia
,
fanconi syndrome
,
sezary syndrome
,
mycosis fungoides
,
necrosis
,
reperfusion injury
,
melanoma
,
nasopharyngeal neoplasms
,
non-small-cell lung carcinoma
,
lung neoplasms
,
type 1 diabetes mellitus
,
refractory anemia with excess of blasts
,
autoimmune diseases
,
ovarian epithelial carcinoma
,
nasopharyngeal carcinoma
,
colorectal neoplasms
,
head and neck neoplasms
,
intestinal neoplasms
,
immunologic deficiency syndromes
,
t-cell leukemia
,
enteropathy-associated t-cell lymphoma
,
mycoses
,
extranodal nk-t-cell lymphoma
,
lymphoproliferative disorders
,
plasmablastic lymphoma
,
refractory anemia
,
prolymphocytic leukemia
,
b-cell leukemia
,
essential thrombocythemia
,
neutrophilic leukemia chronic
,
pancytopenia
,
bone marrow failure disorders
,
glucose intolerance
,
promyelocytic leukemia acute
,
coronavirus
,
amyotrophic lateral sclerosis
,
immune system diseases
,
heart valve diseases
,
aggression
,
reactive arthritis
,
neutropenia
,
chronic granulomatous disease
,
leukocyte-adhesion deficiency syndrome
,
erythema nodosum
,
synovitis
,
diamond-blackfan anemia
,
thymoma
,
thymus neoplasms
,
adult t-cell leukemia-lymphoma
,
megakaryoblastic leukemia acute
,
monocytic leukemia acute
,
myelomonocytic leukemia acute
,
erythroblastic leukemia acute
,
lymphomatoid granulomatosis
,
motor activity
,
hematologic diseases
,
polycythemia vera
,
large granular lymphocytic leukemia
,
peritoneal neoplasms
,
digeorge syndrome
,
kaposi sarcoma
,
kasabach-merritt syndrome
,
hemangioendothelioma
,
pulmonary arterial hypertension
,
seizures
,
meningitis
,
leukemia myeloid chronic atypical bcr-abl negative
,
gestational trophoblastic disease
,
testicular neoplasms
,
trophoblastic neoplasms
,
hairy cell leukemia
,
hemolysis
,
pure red-cell aplasia
,
leukocytoclastic vasculitis cutaneous
,
paroxysmal hemoglobinuria
,
hemoglobinuria
,
optic nerve injuries
,
endometrial neoplasms
,
post-cardiac arrest syndrome
,
squamous cell neoplasms
,
chronic chemical and drug induced liver injury
,
osteoporosis
,
atherosclerosis
,
intranasal administration
,
myocardial infarction
,
paranasal sinus diseases
,
glioblastoma
,
neuromuscular diseases
,
autoimmune thyroiditis
,
radiation injuries
,
bone marrow transplantation
,
homologous transplantation
,
autologous transplantation
,
aphthous stomatitis
,
blastic plasmacytoid dendritic cell neoplasm
,
small cell lung carcinoma
,
rhabdomyosarcoma
,
wilms tumor
,
stomatitis
,
oral ulcer
,
animal mammary neoplasms
,
gastrointestinal stromal tumors
,
exanthema
,
skin neoplasms
,
gastroenteritis
,
renal cell carcinoma
,
spondylarthropathies
,
pheochromocytoma
,
adult-onset still's disease
,
primary immunodeficiency diseases
,
suicide
,
hiv
,
hiv seropositivity
,
intraocular lymphoma
,
monosomy
,
plasma cell leukemia
,
epidermolysis bullosa
,
intestinal obstruction
,
hypocalcemia
,
hypoparathyroidism
,
phenylketonurias
,
mast-cell leukemia
,
h1n1 subtype influenza a virus
,
psychotic affective disorders
,
obsessive-compulsive disorder
,
compulsive behavior
,
paranoid schizophrenia
,
lysosomal storage diseases
,
stiff-person syndrome
,
frontotemporal dementia
,
epithelioid hemangioendothelioma
,
arteriovenous malformations
,
fallopian tube neoplasms
,
rare diseases
,
aids-related lymphoma
,
salivary gland neoplasms
,
postmenopause
,
mucopolysaccharidosis vi
,
mucopolysaccharidoses
,
mucopolysaccharidosis i
,
alpha-mannosidosis
,
mucolipidoses
,
mannosidase deficiency diseases
,
neurotoxicity syndromes
,
triple negative breast neoplasms
,
adenocarcinoma
,
ovarian hyperstimulation syndrome
,
nervous system trauma
,
squamous cell carcinoma of head and neck
,
squamous cell carcinoma
,
ventilator-associated pneumonia
,
drug resistant epilepsy
,
oropharyngeal neoplasms
,
cranial nerve diseases
,
limb-girdle muscular dystrophies
,
leber congenital amaurosis
,
laryngostenosis
,
acanthamoeba keratitis
,
tic disorders
,
hypercholesterolemia
,
opioid-related disorders
,
cocaine-related disorders
,
appendicitis
,
memory disorders
,
fistula
,
neointima
,
hemodynamics
,
hyperalgesia
,
noise-induced hearing loss
,
pelvic girdle pain
,
pathologic processes
,
lipoma
,
hantavirus pulmonary syndrome
,
hantavirus infections
,
glycogen storage disease
,
hepatic encephalopathy
,
magnetic resonance imaging
,
radiodermatitis
,
anosmia
,
stomach neoplasms
,
biliary tract neoplasms
,
neoadjuvant therapy
,
dna repair-deficiency disorders
,
intussusception
,
st elevation myocardial infarction
,
myocardial reperfusion injury
,
ear diseases
,
otorhinolaryngologic diseases
,
unilateral hearing loss
,
radiotherapy
,
cognition disorders
,
postpartum depression
,
depression
,
depressive disorder
,
meningoencephalitis
,
central nervous system tuberculosis
,
no-reflow phenomenon
,
paraneoplastic syndromes
,
bone diseases
,
geographic atrophy
,
chondrocalcinosis
,
ankle injuries
,
tendon injuries
,
foot injuries
,
diet therapy
,
nutrition assessment
,
structural myopathies congenital
,
subarachnoid hemorrhage
,
coronary artery disease
,
mandibular fractures
,
graft vs host disease
,
large b-cell lymphoma diffuse
,
non-hodgkin lymphoma
,
myelodysplastic syndromes
,
b-cell lymphoma
,
plasma cell neoplasms
,
preleukemia
,
b-cell chronic lymphocytic leukemia
,
myeloid leukemia acute
,
alcoholic hepatitis
,
neuromyelitis optica
,
plasmacytoma
,
myeloid leukemia
,
aplastic anemia
,
anemia
,
neoplasm metastasis
,
hematologic neoplasms
,
large-cell lymphoma immunoblastic
,
radiculopathy
,
pulmonary fibrosis
,
myocarditis
,
tuberculosis
,
bronchiolitis obliterans syndrome
,
chronic progressive multiple sclerosis
,
idiopathic pulmonary fibrosis
,
biphenotypic leukemia acute
,
carcinoma
,
precursor t-cell lymphoblastic leukemia-lymphoma
,
bcr-abl positive chronic myelogenous leukemia
,
allergic bronchopulmonary aspergillosis
,
arteritis
,
viral pneumonia
,
heart failure
,
hiv infections
,
optic nerve diseases
,
spinal cord injuries
,
acute disease
,
acquired immunodeficiency syndrome
,
hip osteoarthritis
,
intervertebral disc displacement
,
deglutition disorders
,
interdigitating dendritic cell sarcoma
,
autoimmune diseases of the nervous system
,
leprosy
,
myositis
,
dermatomyositis
,
keratitis
,
aspergillosis
,
open-angle glaucoma
,
post-acute covid-19 syndrome
,
precursor b-cell lymphoblastic leukemia-lymphoma
,
critical illness
,
mucocutaneous lymph node syndrome
,
focal segmental glomerulosclerosis
,
liver neoplasms
,
end stage liver disease
,
langerhans-cell histiocytosis
,
sacroiliitis
,
tennis elbow
,
herpes simplex
,
pulmonary aspergillosis
,
virus diseases
,
ischemia
,
ischemic optic neuropathy
,
hepatocellular carcinoma
,
organ transplantation
,
lung injury
,
histiocytosis
,
sickle cell anemia
,
urinary tract infections
,
sarcoma
,
systemic vasculitis
,
gaucher disease
,
eye infections
,
takayasu arteritis
,
aortic arch syndromes
,
pemphigus
,
hemolytic anemia autoimmune
,
hemolytic anemia
,
exophthalmos
,
peripheral nervous system diseases
,
pneumocystis
,
coronaviridae infections
,
nidovirales infections
,
rna virus infections
,
congenital heart defects
,
psoriasis
,
transverse myelitis
,
alcoholic liver diseases
,
ankylosing spondylitis
,
lymphadenitis
,
contact dermatitis
,
diabetes insipidus
,
biliary atresia
,
therapeutics
,
cardiomyopathies
,
down syndrome
,
tendon entrapment
,
hyperlipoproteinemia type i
,
retinal vasculitis
,
hiccup
,
trismus
,
minor planets
,
polymyositis
,
gangliosidoses
,
dyskeratosis congenita
,
adenoviridae infections
,
macrophage activation syndrome
,
spontaneous remission
,
respiratory tract diseases
,
cardiotoxicity
,
urogenital neoplasms
,
endodontics
,
immunocompromised host
,
cancer pain
,
bacterial pneumonia
,
vertigo
,
spinal cord diseases
,
ornithine carbamoyltransferase deficiency disease
,
vascular remodeling
,
spondylarthritis
,
spondylitis
,
disease
,
pericarditis
,
meniere disease
,
laryngeal edema
,
secondary headache disorders
,
prescription drug overuse
,
meningeal tuberculosis
,
venous thrombosis
,
human herpesvirus 4
,
postherpetic neuralgia
,
central nervous system neoplasms
,
immunoglobulin variable region
,
chorioretinitis
,
hyperplasia
,
adrenogenital syndrome
,
paresis
,
aphasia
,
idiopathic interstitial pneumonias
,
bronchopulmonary dysplasia
,
posterior uveitis
,
panuveitis
,
graft vs host reaction
,
benign mucous membrane pemphigoid
,
intermediate uveitis
,
diabetes complications
,
neurogenic arthropathy
,
abdominal pain
,
neuronal ceroid-lipofuscinoses
,
fucosidosis
,
globoid cell leukodystrophy
,
metachromatic leukodystrophy
,
niemann-pick diseases
,
type a niemann-pick disease
,
adrenoleukodystrophy
,
wolman disease
,
inborn errors metabolism
,
tay-sachs disease
,
sandhoff disease
,
gm1 gangliosidosis
,
type c niemann-pick disease
,
pick disease of the brain
,
croup
,
laryngitis
,
bites and stings
,
hemorrhoids
,
orbital pseudotumor
,
vocal cord paralysis
,
aging
,
spondylosis
,
hyperthyroidism
,
eosinophilic granuloma
,
hypereosinophilic syndrome
,
subdural hematoma
,
subdural hematoma chronic
,
orthostatic intolerance
,
hepatorenal syndrome
,
nontuberculous mycobacterium infections
,
respiration disorders
,
celiac disease
,
skin diseases
,
seborrheic dermatitis
,
ascites
,
tuberculous pericarditis
,
intracranial hemorrhages
,
diffuse cerebral sclerosis of schilder
,
encephalomyelitis
,
acute disseminated encephalomyelitis
,
aids-related opportunistic infections
,
hand injuries
,
finger injuries
,
dilated cardiomyopathy
,
sudden death cardiac
,
left ventricular dysfunction
,
ventricular remodeling
,
microvascular angina
,
exercise tolerance
,
sjogren's syndrome
,
language disorders
,
toxic optic neuropathy
,
erythropoietic protoporphyria
,
glucose metabolism disorders
,
glycogen storage disease type i
,
erythema
,
erythema multiforme
,
ventricular dysfunction
,
anterior cruciate ligament injuries
,
pyoderma gangrenosum
,
x-linked bulbo-spinal atrophy
,
cerebral infarction
,
postthrombotic syndrome
,
acute-on-chronic liver failure
,
acoustic neuroma
,
neurilemmoma
,
human adenovirus infections
,
human influenza
,
psittacosis
,
lymphoma
,
leukemia
,
precursor cell lymphoblastic leukemia-lymphoma
,
syndrome
,
prostatic neoplasms
,
rheumatoid arthritis
,
covid-19
,
kidney transplantation
,
inflammation
,
asthma
,
multiple sclerosis
,
multiple myeloma
,
osteoarthritis
,
lymphoid leukemia
,
cataract
,
neoplasms
,
pneumonia
,
arthritis
,
follicular lymphoma
,
graves ophthalmopathy
,
kidney diseases
,
lupus nephritis
,
knee osteoarthritis
,
hodgkin disease
,
sclerosis
,
recurrence
,
postoperative pain
,
chronic obstructive pulmonary disease
,
systemic lupus erythematosus
,
eye diseases
,
nephrotic syndrome
,
iga glomerulonephritis
,
castration-resistant prostatic neoplasms
,
nephritis
,
hepatitis
,
hepatitis a
,
burkitt lymphoma
,
low back pain
,
healthy volunteers/patients
,
uveitis
,
relapsing-remitting multiple sclerosis
,
adrenal insufficiency
,
respiratory distress syndrome
,
pain
,
hemophagocytic lymphohistiocytosis
,
membranous glomerulonephritis
,
glomerulonephritis
,
giant cell arteritis
,
polymyalgia rheumatica
,
chronic kidney failure
,
renal insufficiency
,
crohn disease
,
vasculitis
,
graft rejection
,
infections
,
macular edema
,
obstructive lung diseases
,
disease progression
,
bursitis
,
thrombocytopenic purpura idiopathic
,
hypersensitivity
,
hearing loss
,
ulcerative colitis
,
large-cell lymphoma anaplastic
,
lung diseases
,
colitis
,
carpal tunnel syndrome
,
breast neoplasms
,
headache
,
edema
,
granulomatosis with polyangiitis
,
coronavirus infections
,
diabetes mellitus
,
chronic renal insufficiency
,
postoperative complications
,
liver transplantation
,
immunosuppression therapy
,
replacement arthroplasty knee
,
deafness
,
nephrosis
,
lipoid nephrosis
,
severe acute respiratory syndrome
,
community-acquired pneumonia
,
fibrosis
,
back pain
,
nasal polyps
,
glaucoma
,
autoimmune hepatitis
,
facial paralysis
,
bell palsy
,
microscopic polyangiitis
,
optic neuritis
,
heart arrest
,
acute lung injury
,
shoulder pain
,
plantar fasciitis
,
sudden hearing loss
,
systemic scleroderma
,
anti-neutrophil cytoplasmic antibody-associated vasculitis
,
pain management
,
cytokine release syndrome
,
psychology rejection
,
stroke
,
chronic pain
,
liver diseases
,
allergic conjunctivitis
,
wounds and injuries
,
dermatitis
,
anterior uveitis
,
atopic dermatitis
,
thrombocytopenia
,
communicable diseases
,
chemical and drug induced liver injury
,
diffuse scleroderma
,
hemangioma
,
proteinuria
,
migraine disorders
,
intervertebral disc degeneration
,
sinusitis
,
inflammatory bowel diseases
,
pneumocystis pneumonia
,
sciatica
,
iridocyclitis
,
retinal diseases
,
postoperative nausea and vomiting
,
infantile spasms
,
insulin resistance
,
ulcer
,
sarcoidosis
,
conjunctivitis
,
agnosia
,
tendinopathy
,
liver failure
,
newborn respiratory distress syndrome
,
infertility
,
ischemic stroke
,
epstein-barr virus infections
,
drug-related side effects and adverse reactions
,
respiratory sounds
,
muscle weakness
,
dry eye syndromes
,
cataract extraction
,
keratoconus
,
rhinosinusitis
,
purpura
,
juvenile arthritis
,
pathologic constriction
,
graves disease
,
neuritis
,
sensorineural hearing loss
,
paralysis
,
interstitial lung diseases
,
hepatic insufficiency
,
vomiting
,
type 2 diabetes mellitus
,
epilepsy
,
emergencies
,
heart transplantation
,
spinal stenosis
,
gout
,
rhinitis
,
systemic inflammatory response syndrome
,
thrombocytopenic purpura
,
status asthmaticus
,
spasm
,
behcet syndrome
,
respiratory tract infections
,
iga vasculitis
,
pulpitis
,
immunoglobulin g4-related disease
,
hemorrhage
,
shoulder impingement syndrome
,
eczema
,
thyroid diseases
,
fasciitis
,
esophageal stenosis
,
duchenne muscular dystrophy
,
muscular dystrophies
,
facies
,
brain neoplasms
,
cognitive dysfunction
,
respiratory insufficiency
,
biliary liver cirrhosis
,
myasthenia gravis
,
allergic rhinitis
,
corneal edema
,
diabetic retinopathy
,
polyps
,
joint diseases
,
hepatitis b
,
hypertension
,
schizophrenia
,
psychotic disorders
,
sepsis
,
cardiopulmonary bypass
,
out-of-hospital cardiac arrest
,
cholangitis
,
extrinsic allergic alveolitis
,
trigger finger disorder
,
musculoskeletal diseases
,
acute liver failure
,
nausea
,
mycoplasma pneumonia
,
mycoplasma pneumoniae
,
liver cirrhosis
,
thrombotic thrombocytopenic purpura
,
granulomatous mastitis
,
mastitis
,
tenosynovitis
,
neuralgia
,
retinal detachment
,
bullous pemphigoid
,
encephalitis
,
bone fractures
,
congenital adrenal hyperplasia
,
fatigue
,
hyperglycemia
,
myelitis
,
hematopoietic stem cell transplantation
,
churg-strauss syndrome
,
capsule opacification
,
heart diseases
,
hypoxia
,
mental disorders
,
anesthesia
,
bacterial infections
,
keratoconjunctivitis sicca
,
acute kidney injury
,
cardiac surgical procedures
,
ocular hypertension
,
spontaneous abortion
,
habitual abortion
,
obstructive sleep apnea
,
sleep apnea syndromes
,
vestibular neuronitis
,
herpetic keratitis
,
hematoma
,
aortic dissection
,
multiple organ failure
,
alopecia areata
,
alopecia
,
psoriatic arthritis
,
renal dialysis
,
delayed graft function
,
parkinson disease
,
restless legs syndrome
,
post-concussion syndrome
,
retinal vein occlusion
,
macular degeneration
,
blister
,
acute pain
,
cytomegalovirus infections
,
meibomian gland dysfunction
,
treatment outcome
,
patient preference
,
corneal transplantation
,
eye pain
,
intraocular pressure
,
epiretinal membrane
,
vitreoretinal surgery
,
pterygium
,
refractive surgical procedures
,
radius fractures
,
drug interactions
,
hypoglycemia
,
demyelinating diseases
,
hemophilia a
,
polyarteritis nodosa
,
chronic disease
,
interstitial nephritis
,
nervous system diseases
,
muscle cramp
,
toxemia
,
retroperitoneal fibrosis
,
muscular diseases
,
post-traumatic headache
,
otitis media
,
otitis
,
otitis media with effusion
,
allergic rhinitis seasonal
,
aortic valve stenosis
,
patient satisfaction
,
pulmonary eosinophilia
,
patient compliance
,
cluster headache
,
facial nerve diseases
,
emphysema
,
pulmonary sarcoidosis
,
oral lichen planus
,
lichen planus
,
rotator cuff tear arthropathy
,
aortic aneurysm
,
arthralgia
,
fuchs' endothelial dystrophy
,
atrial fibrillation
,
chronic hepatitis b
,
chronic hepatitis
,
bronchiolitis
,
apnea
,
connective tissue diseases
,
bundle-branch block
,
ultrasonography
,
ganglion cysts
,
synovial cyst
,
cerebral hemorrhage
,
renal replacement therapy
,
rh isoimmunization
,
neurosurgical procedures
,
elbow fractures
,
penetrating keratoplasty
,
vitrectomy
,
papilledema
,
viral encephalitis
,
wrist fractures
,
orthopedic procedures
,
caregiver burden
,
mediastinal neoplasms
,
cough
,
chronic cough
,
leukoencephalopathies
,
progressive multifocal leukoencephalopathy
,
immune reconstitution inflammatory syndrome
,
mydriasis
,
immunity
,
transplantation
,
hepatitis c
,
sarcopenia
,
neuromuscular monitoring
,
intraoperative complications
,
pseudophakia
,
septic shock
,
shock
,
rolandic epilepsy
,
corneal diseases
,
severe acute respiratory syndrome-related coronavirus
,
lacrimal apparatus diseases
,
borrelia infections
,
fasting
,
vitamin a deficiency
,
night blindness
,
corneal opacity
,
vestibular diseases
,
tracheal stenosis
,
operative surgical procedures
,
viral bronchiolitis
,
polycystic ovary syndrome
,
thoracic aortic aneurysm
,
thoracoabdominal aortic aneurysm
,
delirium
,
hip fractures
,
physiological stress
,
barrett esophagus
,
esophageal diseases
,
chronic bronchitis
,
pituitary diseases
,
fertilization in vitro
,
hysterectomy
,
pudendal neuralgia
,
corneal ulcer
,
bacterial eye infections
,
optic disk drusen
,
regional blood flow
,
mastectomy
,
seroma
,
severe fever with thrombocytopenia syndrome
,
spinal fusion
,
gouty arthritis
,
neoplasms by histologic type
,
dupuytren contracture
,
contracture
,
connective and soft tissue neoplasms
,
connective tissue neoplasms
,
fibroma
,
fibrous tissue neoplasms
,
esophageal neoplasms
,
myalgia
,
paresthesia
,
asthenia
,
aortic valve disease
,
medication adherence
,
arteriosclerosis
,
guillain-barre syndrome
,
heart block
,
contusions
,
nasal obstruction
,
intra-articular injections
,
transcatheter aortic valve replacement
,
traumatic brain injuries
,
anaphylaxis
,
food hypersensitivity
,
cerebrovascular disorders
,
hemorrhagic stroke
,
intracranial aneurysm
,
morton neuroma
,
rotator cuff injuries
,
regeneration
,
mycoplasma infections
,
pleuropneumonia
,
keratoconjunctivitis
,
cicatrix
,
blood pressure
,
vitiligo
,
uveomeningoencephalitic syndrome
,
wound healing
,
neuroma
,
fetal diseases
,
lymph node tuberculosis
,
delayed emergence from anesthesia
,
common cold
,
primary headache disorders
,
lung transplantation
,
hypertrophic cicatrix
,
keloid
,
hypertrophy
,
chronic urticaria
,
urticaria
,
scleritis
,
drug hypersensitivity
,
uveal diseases
,
non-alcoholic fatty liver disease
,
fatty liver
,
herpesviridae infections
,
viremia
,
venous thromboembolism
,
thromboembolism
,
blood coagulation
,
wiskott-aldrich syndrome
,
severe combined immunodeficiency
,
agammaglobulinemia
,
type 1 hyper-igm immunodeficiency syndrome
,
chediak-higashi syndrome
,
common variable immunodeficiency
,
hyper-igm immunodeficiency syndrome
,
pathologic complete response
,
secondary hyperparathyroidism
,
analgesia
,
post-dural puncture headache
,
hashimoto disease
,
menorrhagia
,
hyperaldosteronism
,
hypokalemia
,
sleep initiation and maintenance disorders
,
intraabdominal infections
,
healthcare-associated pneumonia
,
methicillin-resistant staphylococcus aureus
,
bradycardia
,
staphylococcal infections
,
general anesthesia
,
gram-negative bacterial infections
,
bacterial meningitis
,
endocarditis
,
central nervous system infections
,
neuromuscular blockade
,
adenoviridae
,
hyperkinesis
,
cytomegalovirus retinitis
,
port-wine stain
,
simplexvirus
,
retinitis
,
capillary hemangioma
,
bipolar disorder
,
autistic disorder
,
anxiety
,
fibrinolysis
,
treatment-resistant schizophrenia
,
potassium deficiency
,
tonsillectomy
,
male genital diseases
,
male genital neoplasms
,
genital diseases
,
exfoliation syndrome
,
failed back surgery syndrome
,
genes
,
brain death
,
cardiac conduction system disease
,
benign paroxysmal positional vertigo
,
leg injuries
,
vision disorders
,
choroid diseases
,
low vision
,
localized scleroderma
,
bone cysts
,
cysts
,
hypoventilation
,
albuminuria
,
acupuncture therapy
,
dentofacial deformities
,
malignant mesothelioma
,
cochlear implants
,
cholestasis
,
rheumatic diseases
,
rheumatic fever
,
collagen diseases
,
ventral hernia
,
hernia
,
injections
,
iritis
,
femur head necrosis
,
disease susceptibility
,
angle-closure glaucoma
,
hypospadias
,
tissue adhesions
,
atrial flutter
,
scleral buckling
,
poisoning
,
cardiovascular diseases
,
cardiovascular abnormalities
,
orthostatic hypotension
,
hypothermia
,
foot and mouth disease hand
,
ototoxicity
,
electroretinography
,
abdominal aortic aneurysm
,
low cardiac output
,
pleurisy
,
pleural tuberculosis
,
corneal neovascularization
,
pathologic neovascularization
,
pediatric obesity
,
esophageal squamous cell carcinoma
,
root canal obturation
,
oral surgery
,
interstitial cystitis
,
cystitis
,
somatoform disorders
,
cartilage diseases
,
pancreatic neoplasms
,
pets
,
intravenous administration
,
nociceptive pain
,
eosinophilia
,
thrombosis
,
intracranial thrombosis
,
candidiasis
,
cryptococcosis
,
pneumocystis infections
,
humans
,
transcranial direct current stimulation
,
double-blind method
,
risk factors
,
organ dysfunction scores
,
femoracetabular impingement
,
local anesthesia
,
drug-induced abnormalities
,
respiratory aspiration
,
noninvasive ventilation
,
lymphadenopathy
,
cushing syndrome
,
adrenocortical hyperfunction
,
sleep wake disorders
,
parasomnias
,
healthy diet
,
angina pectoris
,
variant angina pectoris
,
radiofrequency ablation
,
hypoalbuminemia
,
impacted tooth
,
hyperbilirubinemia
,
rhinoplasty
,
recovery of function
,
cns demyelinating autoimmune diseases
,
premedication
,
four-dimensional computed tomography
,
emergence delirium
,
mortality
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