PTC Therapeutics - PharmaKB

Company Reports

Company Reports

Disease Reports

Disease Reports

Company ReportsPTC Therapeutics

PTC Therapeutics(PTCT)

PTC Therapeutics is a US pharmaceutical company focused on the development of orally administered small molecule drugs and gene therapy which regulate gene expression by targeting post-transcriptional control (PTC) mechanisms in orphan diseases.

Download report

Favorite

Financial

Marketed Drugs

Clinical Trials

Financial

Stock price

*Currency in USD

Company Revenue

Quarterly

Quarterly

Annual

Annual

Projections

*Quarterly sales USD (in millions)

Plot placeholder

Mock data
Subscribe for the real data

Revenue by Drug

Marketed Drugs

Therapeutic Areas:

All

Classification:

All

Include Generics:

Trade Name	Drug Name	Approved	Patent Expires	Indication
Emflaza	Deflazacort	2017-02-09		Inflammation , Duchenne muscular dystrophy
Translarna	Ataluren	2014-07-31		Duchenne muscular dystrophy
Upstaza	Eladocagene exuparvovec	2022-07-18		Inborn errors amino acid metabolism

Clinical Trials

Therapeutic Areas:

All

Classification:

All

Approval:

All

Status:

All

Phases:

All

Drug Name

Phase 1

Phase 2

Phase 3

Phase 4

Indication

ELADOCAGENE EXUPARVOVEC

argininosuccinic aciduria

,

friedreich ataxia

,

cerebellar ataxia

,

mitochondrial diseases

,

,

,

,

,

diffuse cerebral sclerosis of schilder

,

drug resistant epilepsy

,

,

breast neoplasms

,

central nervous system neoplasms

,

nervous system neoplasms

,

,

myeloid leukemia acute

,

myeloid leukemia

,

,

,

neurofibromatosis 2

,

neurofibromatosis 1

,

neurofibromatoses

,

,

,

coronavirus infections

,

,

,

healthy volunteers/patients

,

b-cell chronic lymphocytic leukemia

,

,

colonic neoplasms

,

non-hodgkin lymphoma

,

large b-cell lymphoma diffuse

,

b-cell lymphoma

,

knee osteoarthritis

,

,

,

,

rectal neoplasms

,

lymphoid leukemia

,

squamous cell carcinoma of head and neck

,

squamous cell carcinoma

,

,

glycogen storage disease

,

,

deficiency diseases

,

essential thrombocythemia

,

polycythemia vera

,

,

,

,

,

falciparum malaria

,

hereditary nephritis

,

,

,

,

viral hemorrhagic fevers

,

,

,

precursor cell lymphoblastic leukemia-lymphoma

,

,

langerhans-cell histiocytosis

,

hypersensitivity

,

peanut hypersensitivity

,

allergic rhinitis

,

,

esophageal neoplasms

,

stomach neoplasms

,

,

myeloid leukemia acute

,

myeloid leukemia

,

colorectal neoplasms

,

prostatic neoplasms

,

venous thromboembolism

,

thromboembolism

,

primary myelofibrosis

,

hypercholesterolemia

,

gaucher disease

,

head and neck neoplasms

,

rheumatoid arthritis

,

,

hematologic neoplasms

,

,

,

thyroid neoplasms

,

thyroid diseases

,

multiple myeloma

,

plasma cell neoplasms

,

,

multiple sclerosis

,

relapsing-remitting multiple sclerosis

,

,

,

tay-sachs disease

,

sandhoff disease

,

,

,

,

haemophilus influenzae type b

,

,

,

neurotoxicity syndromes

,

brugada syndrome

,

chronic kidney failure

,

renal insufficiency

,

type 2 diabetes mellitus

,

diabetes mellitus

,

type 1 diabetes mellitus

,

glycogen storage disease type ii

,

,

atopic dermatitis

,

,

,

,

human influenza

,

,

,

,

,

atrial fibrillation

,

,

,

meningococcal infections

,

,

sedentary behavior

,

,

wounds and injuries

,

heart transplantation

,

reperfusion injury

,

,

,

clostridium infections

,

,

chronic renal insufficiency

,

kidney diseases

,

cardiovascular diseases

,

,

,

hyperlipidemias

,

gastrointestinal stromal tumors

,

,

iron-deficiency anemia

,

iron deficiencies

,

,

,

,

small cell lung carcinoma

,

healthy volunteers/patients

,

,

primary myelofibrosis

,

myeloid leukemia acute

,

myeloid leukemia

,

,

hepatocellular carcinoma

,

,

plexiform neurofibroma

,

neurofibromatoses

,

,

,

,

chronic obstructive pulmonary disease

,

,

triple negative breast neoplasms

,

,

,

essential thrombocythemia

,

polycythemia vera

,

,

,

lupus nephritis

,

,

inflammatory breast neoplasms

,

prostatic neoplasms

,

precursor cell lymphoblastic leukemia-lymphoma

,

precursor t-cell lymphoblastic leukemia-lymphoma

,

b-cell chronic lymphocytic leukemia

,

lymphoid leukemia

,

,

wiskott-aldrich syndrome

,

bcr-abl positive chronic myelogenous leukemia

,

,

graft vs host disease

,

hematopoietic stem cell transplantation

,

bronchiolitis obliterans syndrome

,

,

hyperlipoproteinemia type ii

,

organ transplantation

,

homozygous familial hypercholesterolemia

,

cryopyrin-associated periodic syndromes

,

myelodysplastic syndromes

,

,

liver transplantation

,

thrombocytopenic purpura idiopathic

,

thrombocytopenic purpura

,

,

parkinson disease

,

,

,

juvenile arthritis

,

,

,

,

hepatitis b virus

,

,

,

,

vision disorders

,

,

pituitary acth hypersecretion

,

acth-secreting pituitary adenoma

,

,

acute coronary syndrome

,

,

,

pulmonary eosinophilia

,

pancreatic neoplasms

,

,

,

kidney transplantation

,

,

hypercholesterolemia

,

,

cardiovascular diseases

,

atherosclerosis

,

chronic kidney failure

,

kidney diseases

,

thrombocytopenia

,

breast neoplasms

,

,

renal insufficiency

,

,

,

,

chronic renal insufficiency

,

,

renal replacement therapy

,

drug-related side effects and adverse reactions

,

heart transplantation

,

polycystic kidney diseases

,

autosomal dominant polycystic kidney

,

,

,

cystic fibrosis

,

pseudomonas infections

,

type 2 diabetes mellitus

,

diabetes mellitus

,

multiple myeloma

,

plasma cell neoplasms

,

transplantation

,

cytomegalovirus infections

,

communicable diseases

,

,

,

,

,

,

,

,

neuroendocrine tumors

,

perivascular epithelioid cell neoplasms

,

,

lactic acidosis

,

,

,

friedreich ataxia

,

cerebellar ataxia

ovarian neoplasms

,

ovarian epithelial carcinoma

,

,

diffuse intrinsic pontine glioma

,

,

healthy volunteers/patients

huntington disease

,

urologic neoplasms

,

,

breast neoplasms

,

non-small-cell lung carcinoma

,

triple negative breast neoplasms

,

squamous cell carcinoma of head and neck

,

transitional cell carcinoma

,

squamous cell carcinoma

,

adenocarcinoma of lung

,

castration-resistant prostatic neoplasms

,

squamous cell carcinoma of head and neck

,

,

prostatic neoplasms

,

,

,

squamous cell carcinoma

,

,

colorectal neoplasms

,

pancreatic neoplasms

,

gastrointestinal neoplasms

,

digestive system neoplasms

,

breast neoplasms

,

non-small-cell lung carcinoma

,

,

malignant fibrous histiocytoma

1

2

>

© 2020-2025 Collaborative Drug Discovery Inc. (CDD) | Terms of Use